Single CRISPR infusion cuts stubborn LDL cholesterol for a year
A single dose of CTX310, a CRISPR-Cas9 therapy, dropped LDL cholesterol by more than half in patients who did not respond to standard drugs. The effect lasted at least a year.
Gene Therapy Products 1 article
Gene Therapy Products covers named therapeutic products that alter gene function through gene addition, gene replacement, genome editing or vector-mediated expression. The group includes in vivo AAV and adenoviral therapies, ex vivo modified hematopoietic stem-cell products, nonviral plasmid approaches and oncolytic vectors. Each tag refers to a specific therapy rather than to gene therapy as a class, so vector type, target gene, route of intervention and disease context remain tied to the correct product.